New Paradigm for Genetically Defined Neurodegeneration

CNS-Directed Gene Therapies for Neurodegenerative Diseases

Jaya Biosciences is a privately held pre-clinical stage life sciences company developing therapies for genetically defined neurodegenerative diseases, including Alzheimer’s, Parkinson’s, and frontotemporal dementia.

neurodegeneration, Alzheimer

Our Lead Therapy

JB111 is an experimental CNS-directed AAV9-mediated PPT1 gene therapy currently being developed for neurodegeneration associated with PPT1 haploinsufficiency (carrier status for loss-of-function mutations in palmitoyl protein thioesterase-1 gene or PPT1 heterozygosity).

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